An RNA aptamer restores defective bone growth in FGFR3-related skeletal dysplasia in mice

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Takeshi Kimura, Michaela Bosakova, Yosuke Nonaka, Eva Hruba, Kie Yasuda, Satoshi Futakaua, Takuo Kubota, Bohumil Fafilek, Tomas Gregor, Sara P. Abraham, Regina Gomolkova, Silvie Belaskova, Martin Pesl, Fabiana Csukasi, Ivan Duran, Masatoshi Fushiwara, Michaela Kavkova, Tomas Zikmund, Josef Kaiser, Marcela Buchtova, Deborah Krakow, Yoshikazu Nakamura, Keiichi Ozono, Pavel Krejci. An RNA aptamer restores defective bone growth in FGFR3-related skeletal dysplasia in mice. DOI: 10.1126/scitranslmed.aba4226. Science Translational Medicine (2021), 13:592.

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